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International Centre for Genetic Engineering and Biotechnology

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Exon Specific U1 snRNA as a therapeutic approach for spinal muscular atrophy

Posted on May 2, 2019November 15, 2019 by Suzanne Kerbavcic

The project has awarded to Human Molecular Genetics Group at ICGEB Trieste, headed by F. Pagani.

Duration: 2016-2019

Donor/funding programme:

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